Gene Therapy

The Process

Gene therapy exploits recombinant gene sequences to treat genetic disease. This advanced therapy has tremendous potential for targeting orphan diseases, often overlooked due their limited therapeutic market. Whether your focus is adeno-associated virus (AAV) vectors, lentiviral vectors, or other gene therapy products, our comprehensive range of solutions will enable you to design, produce, and characterise your Gene Therapy products, increasing accessibility in this field.

Step 1

Present your CONCEPT: a gene sequence to be generated and investigated.

Step 2

Our scientific team evaluates your requirements and prepares an experimental plan.

Step 3

We design, generate, and process your sequences through our quality-controlled workflows.

Step 4

Production cell lines are transfected with the validated sequences. A physical biotherapy or optimised cell line…

Equipment we use for Gene Therapy

Beacon Optofluidic system Bruker Cellular Analysis

High precision, clonal isolation technology that uses light to manipulate individual cells into nanopens. Integrated timelapse microscopy allows assessment of soluble, or membrane bound targets...

Culture Station System Bruker Cellular Analysis

Increase the capacity for knowledge-driven clonal selection using the Culture Station System. Used in partnership with the Beacon Optofluidic system for increased clone isolation and...

Ambr 15 Cell Culture Bioreactor System Sartorius

A high throughput, automated microbioreactor system, allowing 48 parallel cultivations, at 10-15 mL scale. This platform enables selection of the optimal clones, media and feeds...

Ambr 250 High Throughput Sartorius

A high throughput, automated bioreactor system with 24 fully featured single-use 100-250ml mini bioreactors. The system enables process development and process optimization in a reproducible,...

BioProfile FLEX2 Nova Biomedical

Metabolite analyser and cell viability counter. Uses optical measurement and freezing point osmometry for automated metabolomic analysis of Gluc, Lac, Gln, Glu, NH4+, Na+, K+,...

ExPERT STx™ MaxCyte

Scalable static or flow electroporation for high-yield, transgene expression. Transfection of 75,000 - 20 billion cell, faster production of stable clones. ISO-certified and scalable production...


Multiplex marker analysis, cell population enrichment or single cell isolation based on

SeqStudio Genetic Analyzer Applied Biosystems

Sequence confirmation using Sanger sequencing and fragment analysis for De novo sequencing, Targeted sequencing Plasmid Sanger sequencing, CRISPR-Cas9 genome editing confirmation, Cell line authentication Detection...

QuantStudio Absolute Q Applied Biosystems

Digital droplet PCR for absolute quantification of nucleic acid sequences. Offers improved inhibitor tolerance, precision, reproducibility and sensitivity relative to standard PCR. 

QuantStudio 7 Pro Applied Biosystems

A real-time PCR system for quantification of nucleic acid sequences. The system offers RFID-enabled workflows, interchangeable blocks (96 and 384-well) and remote monitoring.

Kilobaser one Kilobaser

A desktop DNA Printer. Rapid, reliable oligo sequence synthesis up to 50 bases in length to support your evolving research needs.

TapeStation 4200 Agilent

Automated electrophoresis platform for nucleic acid and protein sample quality evaluation.

Unlock the potential of your research. CONCEPT is equipped with next-generation instrumentation and supports to accelerate research into the next wave of innovative therapies. Let’s turn your CONCEPT into realty with our biotherapy research solutions